Genetic Conditions

Genetic Conditions

Genetic conditions are caused by changes or mutations in genes. These can be inherited or occur spontaneously. Advances in gene therapy and precision medicine are opening new treatment possibilities for many genetic disorders.

How Trials & Therapies Relate

Clinical trials for genetic conditions are testing revolutionary approaches including:

• CRISPR gene editing therapies
• Gene replacement therapy
• Stem cell and cell-based therapies
• Precision medicine and personalized treatments